Question

What is gene therapy? Name the first clinical case in which it was used.

 

 

Answer 1

Gene therapy is a medical technique, used to deal with genetic or congenital diseases. This therapy aims at correction of a genetic defect by delivery of a normal gene to an individual to take over or compensate the function of a non-functional gene.
Gene therapy was first used to treat a four-year old girl suffering from ADA (Adenosine deaminase) deficiency.