Question

Name the gene involved in this therapy.

Answer 1

Gene involved: ADA (Adenosine Deaminase) gene.

Process:

1. Bone marrow stem cells are isolated from the patient.
2. A normal ADA gene is introduced into these cells using a retroviral vector.
3. The genetically modified cells are introduced back into the patient's body.
4. These cells produce the ADA enzyme, helping to restore immune function.