Question

Gene Augmentation Therapy is used for which condition?

Options

• Dominant disorders, cancers, infections

• Potential misuse for non-therapeutic genetic enhancement

• Select cardiovascular and neurological disorders

• Recessive disorders (e.g., ADA deficiency)

Answer 1

Gene Augmentation Therapy is used for recessive disorders such as ADA deficiency. It supplements the function that is missing because of the defective gene.