Question

Mention any two acquired disorders for which somatic cell gene therapy is used.

Answer 1

Somatic cell gene therapy is the only feasible option, and clinical trials have already employed for the treatment of acquired disorders such as cancer and rheumatoid arthritis, and blood disorders, including SCID, Gaucher’s disease, familial hypercholesterolemia, haemophilia, phenylketonuria, cystic fibrosis, sickle cell anaemia, Duchenne muscular dystrophy, emphysema, thalassemia, etc.